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Vol 52, No 2 (2021)
Clinical vignette
Published online: 2021-04-29

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Defibrotide in preventing veno-occlusive disease after hematopoietic stem cell transplantation in children with osteopetrosis

Justyna Miśkiewicz-Bujna1, Izabella Miśkiewicz-Migoń1, Monika Rosa1, Karolina Liszka1, Krzysztof Kałwak1
Acta Haematol Pol 2021;52(2):140-141.

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References

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  2. Penna S, Capo V, Palagano E, et al. One disease, many genes: implications for the treatment of osteopetroses. Front Endocrinol (Lausanne). 2019; 10: 85.
  3. Palagano E, Menale C, Sobacchi C, et al. Genetics of osteopetrosis. Curr Osteoporos Rep. 2018; 16(1): 13–25.
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  8. Qureshi A, Marshall L, Lancaster D. Defibrotide in the prevention and treatment of veno-occlusive disease in autologous and allogeneic stem cell transplantation in children. Pediatr Blood Cancer. 2008; 50(4): 831–832.
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  10. Corbacioglu S, Schulz A, Sedlacek P, et al. Defibrotide for prophylaxis of hepatic veno-occlusive disease in pediatric hematopoietic stem cell transplantation: subanalysis data from an open-label, phase III, randomized trial. Blood. 2015; 126(23): 4310–4310.
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