open access

Vol 52, No 2 (2021)
Clinical vignette
Submitted: 2021-04-09
Accepted: 2021-04-09
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Defibrotide in preventing veno-occlusive disease after hematopoietic stem cell transplantation in children with osteopetrosis

Justyna Miśkiewicz-Bujna, Izabella Miśkiewicz-Migoń, Monika Rosa, Karolina Liszka, Krzysztof Kałwak
DOI: 10.5603/AHP.2021.0022
·
Acta Haematol Pol 2021;52(2):140-141.

open access

Vol 52, No 2 (2021)
CLINICAL VIGNETTE
Submitted: 2021-04-09
Accepted: 2021-04-09

Abstract

Not available

Abstract

Not available
Get Citation
About this article
Title

Defibrotide in preventing veno-occlusive disease after hematopoietic stem cell transplantation in children with osteopetrosis

Journal

Acta Haematologica Polonica

Issue

Vol 52, No 2 (2021)

Article type

Clinical vignette

Pages

140-141

DOI

10.5603/AHP.2021.0022

Bibliographic record

Acta Haematol Pol 2021;52(2):140-141.

Authors

Justyna Miśkiewicz-Bujna
Izabella Miśkiewicz-Migoń
Monika Rosa
Karolina Liszka
Krzysztof Kałwak

References (10)
  1. Corbacioglu S, Carreras E, Ansari M, et al. Diagnosis and severity criteria for sinusoidal obstruction syndrome/veno-occlusive disease in pediatric patients: a new classification from the European society for blood and marrow transplantation. Bone Marrow Transplant. 2017; 53(2): 138–145.
  2. Penna S, Capo V, Palagano E, et al. One disease, many genes: implications for the treatment of osteopetroses. Front Endocrinol (Lausanne). 2019; 10: 85.
  3. Palagano E, Menale C, Sobacchi C, et al. Genetics of osteopetrosis. Curr Osteoporos Rep. 2018; 16(1): 13–25.
  4. Orchard PJ, Fasth AL, Le Rademacher J, et al. Hematopoietic stem cell transplantation for infantile osteopetrosis. Blood. 2015; 126(2): 270–276.
  5. Shadur B, Zaidman I, NaserEddin A, et al. Successful hematopoietic stem cell transplantation for osteopetrosis using reduced intensity conditioning. Pediatr Blood Cancer. 2018; 65(6): e27010.
  6. Driessen GJA, Gerritsen EJA, Fischer A, et al. Long-term outcome of haematopoietic stem cell transplantation in autosomal recessive osteopetrosis: an EBMT report. Bone Marrow Transplant. 2003; 32(7): 657–663.
  7. Corbacioglu S, Hönig M, Lahr G, et al. Stem cell transplantation in children with infantile osteopetrosis is associated with a high incidence of VOD, which could be prevented with defibrotide. Bone Marrow Transplant. 2006; 38(8): 547–553.
  8. Qureshi A, Marshall L, Lancaster D. Defibrotide in the prevention and treatment of veno-occlusive disease in autologous and allogeneic stem cell transplantation in children. Pediatr Blood Cancer. 2008; 50(4): 831–832.
  9. Baker DE, Demaris K. Defibrotide. Hosp Pharm. 2016; 51(10): 847–854.
  10. Corbacioglu S, Schulz A, Sedlacek P, et al. Defibrotide for prophylaxis of hepatic veno-occlusive disease in pediatric hematopoietic stem cell transplantation: subanalysis data from an open-label, phase III, randomized trial. Blood. 2015; 126(23): 4310–4310.

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