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Defibrotide in preventing veno-occlusive disease after hematopoietic stem cell transplantation in children with osteopetrosis
Affiliations- Department of Pediatric Bone Marrow Transplantation, Oncology and Hematology, Wrocław Medical University, Wrocław, Poland
open access
Abstract
Abstract
About this articleTitle
Defibrotide in preventing veno-occlusive disease after hematopoietic stem cell transplantation in children with osteopetrosis
Journal
Issue
Article type
Clinical vignette
Pages
140-141
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315
Article views/downloads
378
DOI
10.5603/AHP.2021.0022
Bibliographic record
Acta Haematol Pol 2021;52(2):140-141.
Authors
Justyna Miśkiewicz-Bujna
Izabella Miśkiewicz-Migoń
Monika Rosa
Karolina Liszka
Krzysztof Kałwak
References (10)- Corbacioglu S, Carreras E, Ansari M, et al. Diagnosis and severity criteria for sinusoidal obstruction syndrome/veno-occlusive disease in pediatric patients: a new classification from the European society for blood and marrow transplantation. Bone Marrow Transplant. 2017; 53(2): 138–145.
- Penna S, Capo V, Palagano E, et al. One disease, many genes: implications for the treatment of osteopetroses. Front Endocrinol (Lausanne). 2019; 10: 85.
- Palagano E, Menale C, Sobacchi C, et al. Genetics of osteopetrosis. Curr Osteoporos Rep. 2018; 16(1): 13–25.
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- Corbacioglu S, Hönig M, Lahr G, et al. Stem cell transplantation in children with infantile osteopetrosis is associated with a high incidence of VOD, which could be prevented with defibrotide. Bone Marrow Transplant. 2006; 38(8): 547–553.
- Qureshi A, Marshall L, Lancaster D. Defibrotide in the prevention and treatment of veno-occlusive disease in autologous and allogeneic stem cell transplantation in children. Pediatr Blood Cancer. 2008; 50(4): 831–832.
- Baker DE, Demaris K. Defibrotide. Hosp Pharm. 2016; 51(10): 847–854.
- Corbacioglu S, Schulz A, Sedlacek P, et al. Defibrotide for prophylaxis of hepatic veno-occlusive disease in pediatric hematopoietic stem cell transplantation: subanalysis data from an open-label, phase III, randomized trial. Blood. 2015; 126(23): 4310–4310.